6642. Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial.
作者: Michela Guglieri.;Kate Bushby.;Michael P McDermott.;Kimberly A Hart.;Rabi Tawil.;William B Martens.;Barbara E Herr.;Elaine McColl.;Chris Speed.;Jennifer Wilkinson.;Janbernd Kirschner.;Wendy M King.;Michelle Eagle.;Mary W Brown.;Tracey Willis.;Robert C Griggs.; .;Volker Straub.;Henriette van Ruiten.;Anne-Marie Childs.;Emma Ciafaloni.;Perry B Shieh.;Stefan Spinty.;Lorenzo Maggi.;Giovanni Baranello.;Russell J Butterfield.;I A Horrocks.;Helen Roper.;Zoya Alhaswani.;Kevin M Flanigan.;Nancy L Kuntz.;Adnan Manzur.;Basil T Darras.;Peter B Kang.;Leslie Morrison.;Monika Krzesniak-Swinarska.;Jean K Mah.;Tiziana E Mongini.;Federica Ricci.;Maja von der Hagen.;Richard S Finkel.;Kathleen O'Reardon.;Matthew Wicklund.;Ashutosh Kumar.;Craig M McDonald.;Jay J Han.;Nanette Joyce.;Erik K Henricson.;Ulrike Schara-Schmidt.;Andrea Gangfuss.;Ekkehard Wilichowski.;Richard J Barohn.;Jeffrey M Statland.;Craig Campbell.;Giuseppe Vita.;Gian Luca Vita.;James F Howard.;Imelda Hughes.;Hugh J McMillan.;Elena Pegoraro.;Luca Bello.;W Bryan Burnette.;Mathula Thangarajh.;Taeun Chang.
来源: JAMA. 2022年327卷15期1456-1468页
Corticosteroids improve strength and function in boys with Duchenne muscular dystrophy. However, there is uncertainty regarding the optimum regimen and dosage.
6652. Trends and Outcomes for Preimplantation Genetic Testing in the United States, 2014-2018.
作者: Heather S Hipp.;Sara Crawford.;Sheree Boulet.;James Toner.;Amy A E Sparks.;Jennifer F Kawwass.
来源: JAMA. 2022年327卷13期1288-1290页
This study uses US national surveillance data to describe preimplantation genetic testing trends and outcomes between 2014 and 2018.
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